TY - GEN AU - Pino-Barrio, Maria José AU - Giménez, Yari AU - Villanueva, Mariela AU - Hildenbeutel, Marcus AU - Sánchez-Domínguez, Rebeca AU - Rodriguez Perales, Sandra AU - Pujol, Roser AU - Surrallés, Jordi AU - Río, Paula AU - Cathomen, Toni AU - Mussolino, Claudio AU - Bueren, Juan Antonio AU - Navarro, Susana PY - 2020 DO - 10.1038/s41598-020-63971-z SN - 2045-2322 UR - http://hdl.handle.net/20.500.12105/9789 AB - The promising ability to genetically modify hematopoietic stem and progenitor cells by precise gene editing remains challenging due to their sensitivity to in vitro manipulations and poor efficiencies of homologous recombination. This study represents... LA - eng PB - Nature Publishing Group TI - TALEN mediated gene editing in a mouse model of Fanconi anemia TY - research article ER -