Robustness of Catalytically Dead Cas9 Activators in Human Pluripotent and Mesenchymal Stem Cells

Narrowing the Genetic Causes of Language Dysfunction in the 1q21.1 Microduplication Syndrome

CRISPR/Cas9 for Cancer Therapy: Hopes and Challenges

Somatic genome editing with the RCAS-TVA-CRISPR-Cas9 system for precision tumor modeling

The IS2 Element Improves Transcription Efficiency of Integration-Deficient Lentiviral Vector Episomes

Germline mutations in the spindle assembly checkpoint genes BUB1 and BUB3 are infrequent in familial colorectal cancer and polyposis

CRISPR-Cas9: A Revolutionary Tool for Cancer Modelling

Clinically Relevant Correction of Recessive Dystrophic Epidermolysis Bullosa by Dual sgRNA CRISPR/Cas9-Mediated Gene Editing

Functional characterization of two enhancers located downstream FOXP2

TALEN mediated gene editing in a mouse model of Fanconi anemia